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Mol Ther
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Nat Methods
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Vivien A. C. Schoonenberg, Mitchel A. Cole, Qiuming Yao, Claudio Macias-Treviño, Falak Sher, Patrick G. Schupp, Matthew C. Canver, Takahiro Maeda, Luca Pinello, Daniel E. Bauer
CRISPRO Identifies Functional Protein Coding Sequences Based on Genome Editing Dense Mutagenesis
bioRxiv
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Canver MC, Haeussler M, Bauer DE, Orkin SH, Sanjana NE, Shalem O, Yuan GC, Zhang F, Concordet JP, Pinello L
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Nat Protoc
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An enhancer haplotype may influence BCL11A expression levels and the response to hydroxyurea in β-thalassemia patients.
Pharmacogenomics
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